Miglustat is a drug currently under phase 2 clinical trials on patients suffering from cystic fibrosis. Its potential for treating the disease was discovered in 2006 and researchers can now show that daily, long-term treatment of human cystic fibrosis cells with low doses of miglustat corrects the main pathological abnormalities. They are therefore extremely hopeful that miglustat will prove effective with patients, and become the first drug able to treat the disease rather than the symptoms.